--- title: Cell and Gene Therapy | Discovery description: Cell and gene therapy research and discovery solutions for product development, including assay support, viral vector platforms, and labware. --- [![Azenta Life Sciences](https://web.azenta.com/hubfs/Azenta%20Logo%20and%20Brand%20Assets/Azenta%20Logos/Azenta_Logo_Hubspot_FullColor.svg "Azenta Life Sciences")](https://www.azenta.com) Open main menu Close main menu [HOME](https://web.azenta.com/cell-and-gene-therapy?hsLang=en) [DISCOVERY](https://web.azenta.com/cell-and-gene-therapy/discovery) [PRECLINICAL & CLINICAL](https://web.azenta.com/cell-and-gene-therapy/clinical?hsLang=en) [MANUFACTURING & DISTRIBUTION](https://web.azenta.com/cell-and-gene-therapy/manufacturing?hsLang=en) [CONTACT AN EXPERT](https://web.azenta.com/cell-and-gene-therapy-contact-an-expert?hsLang=en) ![](https://web.azenta.com/hs-fs/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Overview%20Landing%20Page/00_StickyNav/push%20up.png?width=50&name=push%20up.png) # CELL AND GENE THERAPY ## Research and Discovery Solutions Identify cell and gene therapy solutions for your product development programs, including unique structural and functional assay support, viral vector platforms, target identification and characterization, and labware needed for your discovery process [CONTACT US](https://web.azenta.com/cell-and-gene-therapy-contact-an-expert?hsLang=en) ## CELL AND GENE THERAPY DEVELOPMENT ## Accelerate cell and gene therapy *product development* Azenta Life Sciences provides technology innovations and proprietary protocols to bring your cell and gene therapy products to the forefront. Partner with Azenta’s experts to design and generate viral vector packaging for both in vivo and in vitro research. ![Azenta_Discovery_Redefine_Image](https://web.azenta.com/hubfs/Azenta_Discovery_Redefine_Image.png "Azenta_Discovery_Redefine_Image") --- ![Target - Discover](https://web.azenta.com/hs-fs/hubfs/Target%20-%20Discover.png?width=57&height=49&name=Target%20-%20Discover.png "Target - Discover") ### CELL THERAPY & ASSAY DEVELOPMENT  Analyze your disease samples for mutations, and deliver validated drug targets in a variety of therapeutic areas. Services include: [RNA Sequencing](https://www.genewiz.com/Public/Services/Next-Generation-Sequencing/RNA-Seq), [Mutation Analysis](https://www.genewiz.com/Public/Services/Molecular-Genetics/Mutation-Analysis), [Oligo Synthesis](https://www.genewiz.com/en-GB/Public/Services/Oligo), [Cell Line Engineering Confirmation,](https://www.genewiz.com/Public/Services/Molecular-Genetics/cDNA-Verification) and [Integration Site Analysis](https://www.genewiz.com/Public/Services/Clinical-Services/CLIA-Integration-Site-Analysis) --- ![Search - Discover](https://web.azenta.com/hs-fs/hubfs/Search%20-%20Discover.png?width=50&height=48&name=Search%20-%20Discover.png "Search - Discover") ## VIRAL VECTOR PLATFORMS & SEQUENCING Deliver the right vector package for your gene therapy research and workflows. Services include: [RNA Sequencing](https://www.genewiz.com/en-GB/Public/Services/Next-Generation-Sequencing/RNA-Seq), [CRISPR Validation Services,](https://www.genewiz.com/en/Public/Services/Next-Generation-Sequencing/CRISPR-Validation)[gRNA Construct Synthesis](https://www.genewiz.com/en/Public/Services/Gene-Synthesis/CRISPR-Construct-Synthesis), [AAV ITR Sanger Sequencing](https://www.genewiz.com/en/Public/Services/Sanger-Sequencing/AAV-ITR), [Whole AAV Genome Sequencing](https://www.genewiz.com/Public/Services/Next-Generation-Sequencing/AAV-Genome-Sequencing), [Synthetic DNA Solutions, Viral Production Bundle (AAV Packaging, Lentivirus, Baculovirus),](https://www.genewiz.com/en/Public/Services/Gene-Synthesis/Viral-Package)and [Digital PCR (dPCR)](https://www.genewiz.com/Public/Services/Molecular-Genetics/PCR-Solutions) ## **GENE THERAPY AND RARE DISEASES** ## Customer Testimonial: AskBio [![watch_video](https://no-cache.hubspot.com/cta/default/3478602/e2ab4893-006a-45df-8652-2d8a8ad06b4d.png)](https://cta-redirect.hubspot.com/cta/redirect/3478602/e2ab4893-006a-45df-8652-2d8a8ad06b4d) ## CELL AND GENE THERAPY DEVELOPMENT ## AskBio: Leader in the gene therapy space finds *AAV solutions with Azenta*   AskBio is focused on the development of new gene therapy technologies to address debilitating genetic diseases. Their technologies and treatments make significant impacts to patient lives with Azenta’s Adeno-associated virus (AAV) vector solutions helping to overcome product development challenges. ## CELL AND GENE THERAPY CHALLENGES ## Clearing Roadblocks in Early-Stage Cell & Gene Therapy Development Biotech companies are encountering common bottlenecks for discovery and scale-up. Gene therapy vectors like AAV contain features that can interfere with traditional QC methods. However, recent innovations are overcoming these challenges. [READ MORE](https://www.azenta.com/blog/clearing-roadblocks-early-stage-cell-gene-therapy-development) ## CELL AND GENE THERAPY SOLUTIONS ## *Support your entire workflow* with proven and effective cell and gene therapy solutions Azenta Life Sciences offers a full range of compatible solutions to support your cell and gene therapy product development. Please see below for more information on our total cell and gene therapy discovery solutions. - [AAV SOLUTIONS](https://web.azenta.com/cell-and-gene-therapy/discovery#tab-1) - ## AAV Solutions When precision matters, Azenta's suite of AAV solutions help target and manipulate cell types based on expression, location, and connectivity. ![AAV Plasmid Synthesis](https://web.azenta.com/hs-fs/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/04_Products%20and%20Services/WholeAAVGenomeSequencing.png?width=200&name=WholeAAVGenomeSequencing.png) ##### [Whole AAV Genome Sequencing](https://www.genewiz.com/Public/Services/Next-Generation-Sequencing/AAV-Genome-Sequencing) Verify the integrity of packaged AAV vectors, measure AAV expression after infection, and monitor host response. ![AAV-ITR Sanger-1](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/04_Products%20and%20Services/AAV-ITR%20Sanger-1.svg) ##### [AAV-ITR SANGER SEQUENCING](https://www.genewiz.com/Public/Services/Sanger-Sequencing/AAV-ITR/) Utilizes Sanger protocols to sequence-confirm difficult ITR regions, expediting screening and validation of lead candidates. ![AAV Plasmid Synthesis](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/04_Products%20and%20Services/AAV%20Plasmid%20Synthesis.svg) ##### [AAV PLASMID SYNTHESIS](https://www.genewiz.com/Public/Services/Gene-Synthesis/AAV-Plasmid-Synthesis/) The first of its kind, this provides researchers with synthesis and cloning of transgene expression cassettes into custom AAV vectors. ### Cryogenic Lab Equipment Rely on the highest-quality cryogenic consumables and instruments to support research and development for temperature-sensitive applications. ![Cryogenic Consumables](https://web.azenta.com/hs-fs/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/04_Products%20and%20Services/Cryogenic%20Consumables.png?width=129&name=Cryogenic%20Consumables.png) ##### [Cryogenic Sample Tubes](https://www.azenta.com/product-sampletube/sample-tube-consumables-instruments?f%5B0%5D=category_sampletube%3A971) Built for automation, Azenta's tri-coded and dual-coded sample tubes offer tracking, auditing, and data sharing. ![Cryopod](https://web.azenta.com/hs-fs/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/04_Products%20and%20Services/Cryopod.png?width=184&name=Cryopod.png) ##### [CryoPod™ Carrier](https://www.azenta.com/products/cryopod-carrier) The LN2 vapor-based CryoPod Carrier is a portable, lightweight, and portable solution capable of  storing samples at ≤ -150°C for over 3 hours. ![Benchtop Heating & Cooling Solutions](https://web.azenta.com/hs-fs/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/04_Products%20and%20Services/Benchtop%20Heating%20%26%20Cooling%20Solutions.png?width=230&name=Benchtop%20Heating%20%26%20Cooling%20Solutions.png) ##### [Cell Freezing Containers](https://www.azenta.com/products/sample-consumables-instruments?f%5B0%5D=category%3A951) Unbreakable, easy and safe to open when frozen, Azenta's cell freezing containers control the rate of heat removal to provide reproducible results.  ## CELL AND GENE THERAPY RESOURCES ## Resources for your cell and gene therapy *product development* Accelerate your workflow and deliver results with Azenta's comprehensive offering. Have questions? Azenta's team of scientists and experts can provide additional assistance. - [BROCHURES & FLYERS](https://web.azenta.com/cell-and-gene-therapy/discovery#tab-1) - [WEBINARS & VIDEOS](https://web.azenta.com/cell-and-gene-therapy/discovery#tab-2) - [OTHER RESOURCES](https://web.azenta.com/cell-and-gene-therapy/discovery#tab-3) #### RNA Sequencing [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/13002-SD%201221V1%20RNA-Seq%20Sell%20Sheet.pdf?hsLang=en) #### Gene-to-Lentivirus  [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/12003-SD-US%201221%20Gene%20to%20Lentivirus%20Sell%20Sheet%20US.pdf?hsLang=en) #### Gene-to-Baculovirus [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/12002-SD-US%201221%20Gene%20to%20Baculovirus%20Sell%20Sheet%20US.pdf?hsLang=en) #### AAV Genome Sequencing  [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/13003-SD%200424%20AAV%20Genome%20Sequencing%20Sell%20Sheet.pdf?hsLang=en) #### AAV Plasmid Synthesis  [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/12004-SD%201221%20AAV%20Plasmid%20Synthesis%20Sell%20Sheet.pdf?hsLang=en) #### AAV Plasmid Preparation [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/15001-SD%201221V1%20AAV%20Plasmid%20Prep%20Sell%20Sheet.pdf?hsLang=en) #### AAV-ITR Sanger Sequencing  [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/11001-SD%201221%20AAV-ITR%20Sequencing%20Sell%20Sheet.pdf?hsLang=en) #### AAV Packaging [Download PDF >](https://web.azenta.com/hubfs/2022-01%20CGT%20Umbrella/12051-SO%200523%20AAV%20Packaging%20Sell%20Sheet.pdf?hsLang=en) #### CryoPod and Filling Station  [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/37001-SO%201221V1%20CryoPod%20and%20Filling%20Station.pdf?hsLang=en) #### Digital PCR (dPCR)  [Download PDF >](https://web.azenta.com/hubfs/2022-01%20CGT%20Umbrella/11030-SO%200623%20qPCR%20%26%20dPCR%20Sell%20Sheet.pdf?hsLang=en) #### Labware and Consumables  [Download PDF >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Discovery%20Sell%20Sheets/40003-SO%200122V1.pdf?hsLang=en) #### Webinar: Innovative Genomics and Cold Chain Solutions for Cell and Gene Therapy Development [Watch Webinar >](https://web.genewiz.com/innovative-solutions-webinar-1?hsLang=en) #### Webinar: A Comprehensive Guide to Using Adeno-Associated Virus (AAV) Vectors in Gene Therapy [Watch Webinar >](https://hubs.ly/Q016wlD20) #### Webinar: Understanding the Challenges and Opportunities of Biological Sample Cryopreservation [Watch Webinar >](https://hubs.ly/Q016wm820) #### Video: AskBio AAV Solutions in Gene Therapy [Watch Video >](https://web.azenta.com/hubfs/2022%20Cell%20and%20Gene%20Therapy%20Campaign/Discovery%20Page/Azenta_Customer_Video_askbio_profile_final%20(1080p).mp4?hsLang=en) #### Tech Note: Reading Through the Inverted Terminal Repeats (ITRs) of Adeno-Associated Virus (AAV) [Download >](https://web.azenta.com/aav-itr-tech-note?hsLang=en) #### Tech Note: Integration Site Analysis for Long-Term Safety Monitoring of Cell and Gene Therapy Products [Download >](https://www.azenta.com/resources/integration-site-analysis-long-term-safety-monitoring-cell-and-gene-therapy-products) #### Adeno-Associated Virus (AAV) Services [Learn More >](https://www.genewiz.com/en/Public/Research-Areas/AAV) #### Tech Note: An Efficient and High-Fidelity Approach to AAV Plasmid Preparation [Download >](https://web.azenta.com/tech-note/aav-plasmid-prep?hsLang=en) #### Tech Note: An Efficient and High-Fidelity Approach to AAV Packaging [Download >](https://www.azenta.com/resources/efficient-and-reliable-approach-aav-packaging) ## CELL AND GENE THERAPY COMMERCIALIZATION ## Prepare your cell and gene therapy programs for *scalable product development*   ### [Preclinical & Clinic ](https://web.azenta.com/cell-and-gene-therapy/clinical?hsLang=en) #### [VECTOR & CELL BANK CONFIRMATION | CLINICAL TRIALS](https://web.azenta.com/cell-and-gene-therapy/clinical?hsLang=en) ### [Manufacturing & Distribution ](https://web.azenta.com/cell-and-gene-therapy/manufacturing?hsLang=en) #### [MANUFACTURING SCALE-UP | THERAPEUTICS MANAGEMENT](https://web.azenta.com/cell-and-gene-therapy/manufacturing?hsLang=en) ## **CELL AND GENE THERAPY DISCOVERY** ## Subscribe for cell and gene therapy *updates* Want to validate, optimize, or scale up right now? Need to know what's next? Connect with Azenta Life Sciences, leading the way in cell and gene therapy infrastructure and expertise. ![Azenta_Logo_Primary_FullColor_BlackType_RGB_JP](https://web.azenta.com/hs-fs/hubfs/ja-jp/JP_images/Azenta_Logo_Primary_FullColor_BlackType_RGB_JP.png?width=200&height=66&name=Azenta_Logo_Primary_FullColor_BlackType_RGB_JP.png "Azenta_Logo_Primary_FullColor_BlackType_RGB_JP") - - - - Copyright © 2022 Azenta US, Inc.    [Privacy Policy](https://www.azenta.com/privacy-statement)   |   [Cookie Policy](https://www.azenta.com/cookie-policy)   |   [Terms and Conditions](https://www.azenta.com/terms-and-conditions)   |    [Terms of Use](https://www.azenta.com/terms-and-conditions)    |     [Careers](https://careers.azenta.com/)